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\n

\n <\/a><\/p>\n

\n <\/p>\n<\/div>\n

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\u9510\u6b63\u57fa\u56e0\u521b\u59cb\u4eba\u3001\u8463\u4e8b\u957f\u517c\u9996\u5e2d\u6267\u884c\u5b98\u738b\u6c38\u5fe0\u535a\u58eb\u8868\u793a\uff1a”\u5728\u56fd\u9645\u6743\u5a01\u821e\u53f0\u4e0a\u5206\u4eab\u81ea\u4e3b\u7814\u53d1\u7684\u521b\u65b0\u8fdb\u5c55\uff0c\u5bf9\u4e8e\u9510\u6b63\u57fa\u56e0\u6765\u8bf4\uff0c\u65e0\u7591\u662f\u4e00\u4e2a\u91cc\u7a0b\u7891\u5f0f\u7684\u65f6\u523b\u3002\u8fd9\u6807\u5fd7\u7740\u6211\u4eec\u671d\u7740\u5168\u7403\u5316\u7b56\u7565\u7684\u76ee\u6807\u8fc8\u8fdb\u4e86\u91cd\u5927\u4e00\u6b65\u3002\u6211\u4eec\u5c06\u6301\u7eed\u6df1\u5316\u4e0e\u9886\u57df\u5185\u4e13\u5bb6\u7684\u4ea4\u6d41\u5408\u4f5c\uff0c\u671f\u5f85\u5728\u6b64\u6b21\u4f1a\u8bae\u4e0a\u4e0e\u6f5c\u5728\u5408\u4f5c\u4f19\u4f34\u5c55\u5f00\u6df1\u5ea6\u4ea4\u6d41\u3002”<\/p>\n

ASGCT\u6210\u7acb\u4e8e1996\u5e74\uff0c\u662f\u5168\u7403\u57fa\u56e0\u4e0e\u7ec6\u80de\u6cbb\u7597\u9886\u57df\u6700\u5927\u7684\u4e13\u4e1a\u6027\u975e\u8425\u5229\u533b\u5b66\u548c\u79d1\u5b66\u7ec4\u7ec7\uff0c\u5728\u5168\u7403\u62e5\u6709\u8d85\u8fc75000\u540d\u6210\u5458\u3002ASGCT\u5e74\u4f1a\u662f\u5168\u7403\u57fa\u56e0\u4e0e\u7ec6\u80de\u6cbb\u7597\u9886\u57df\u89c4\u6a21\u6700\u5927\u3001\u6700\u5177\u6743\u5a01\u6027\u7684\u5b66\u672f\u4f1a\u8bae\u3002<\/p>\n

\u53e3\u5934\u62a5\u544a\uff1a<\/p>\n

\u6807\u9898\uff1aART001: Development and Interim Clinical Outcomes of a CRISPR-Based In Vivo Gene-Editing Therapy for Hereditary ATTR \/ ART001:\u57fa\u4e8eCRISPR\u6280\u672f\u7684\u4f53\u5185\u57fa\u56e0\u7f16\u8f91\u7597\u6cd5\u6cbb\u7597\u8f6c\u7532\u72b6\u817a\u7d20\u86cb\u767d\u6dc0\u7c89\u6837\u53d8\u6027\uff08ATTR\uff09\u7684\u6700\u65b0\u4e34\u5e8a\u8fdb\u5c55
\u62a5\u544a\u65f6\u95f4\uff1a2025\u5e745\u670816\u65e5\uff08\u661f\u671f\u4e94\uff09\u4e0b\u53485:15-5:30\uff08\u7f8e\u56fd\u4e2d\u90e8\u65f6\u95f4\uff09
\u5730\u70b9\uff1a393-396\u5385
\u6458\u8981\u7f16\u53f7\uff1aAMA434<\/p>\n

\u6d77\u62a5\u5c55\u793a\uff1a<\/p>\n

\u6807\u9898\uff1a Efficacy and Safety of ART002, a Single-dose Gene Editing Therapy, in Patients with Severe Heterozygous Familial Hypercholesterolemia \/ \u4f53\u5185\u57fa\u56e0\u7f16\u8f91\u7597\u6cd5ART002\u9488\u5bf9\u4e25\u91cdHeFH\u60a3\u8005\u3001\u5355\u6b21\u7ed9\u836f\u5b89\u5168\u6027\u4e0e\u6709\u6548\u6027\u7684\u4e34\u5e8a\u6570\u636e
\u6d77\u62a5\u5c55\u793a\u65f6\u95f4\uff1a2025\u5e745\u670813\u65e5\uff08\u661f\u671f\u4e8c\uff09\u4e0b\u53486:00-7:30\uff08\u7f8e\u56fd\u4e2d\u90e8\u65f6\u95f4\uff09
\u5730\u70b9\uff1a\u6d77\u62a5\u5c55\u793a\u5385 Hall I2
\u6458\u8981\u7f16\u53f7\uff1aAMA562<\/p>\n

\u6807\u9898\uff1aEngineering TadA-Derived Base Editors with Enhanced Potency and Safety for non-viral In Vivo Gene Editing \/ \u200c\u57fa\u4e8eTadA\u7684\u589e\u6548\u5b89\u5168\u578b\u78b1\u57fa\u7f16\u8f91\u5668\u7684\u5f00\u53d1\u53ca\u5176\u5728\u975e\u75c5\u6bd2\u4f53\u5185\u57fa\u56e0\u7f16\u8f91\u4e2d\u7684\u5e94\u7528
\u6d77\u62a5\u5c55\u793a\u65f6\u95f4\uff1a2025\u5e745\u670815\u65e5\uff08\u661f\u671f\u56db\uff09\u4e0b\u53485:30-7:00\uff08\u7f8e\u56fd\u4e2d\u90e8\u65f6\u95f4\uff09
\u5730\u70b9\uff1a\u6d77\u62a5\u5c55\u793a\u5385 Hall I2
\u6458\u8981\u7f16\u53f7\uff1aAMA559<\/p>\n

###<\/p>\n

\u5173\u4e8e\u9510\u6b63\u57fa\u56e0<\/p>\n

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\u516c\u53f8\u62e5\u6709\u4e00\u652f\u5177\u5907\u751f\u7269\u836f\u5168\u751f\u547d\u5468\u671f\u6210\u529f\u7ecf\u9a8c\u7684\u4e13\u4e1a\u5316\u56e2\u961f\uff0c\u5efa\u7acb\u4e86\u5168\u7403\u9996\u4e2a\u7ecf\u4e34\u5e8a\u9a8c\u8bc1\u7684\u4ea7\u4e1a\u7ea7\u3001\u7aef\u5230\u7aef\u4f53\u5185\u57fa\u56e0\u7f16\u8f91\u6280\u672f\u5e73\u53f0\uff0c\u7cfb\u7edf\u5e03\u5c40\u4e86\u76f8\u5173\u6280\u672f\u4e0e\u4ea7\u54c1\u77e5\u8bc6\u4ea7\u6743\uff0c\u5176\u4e2d\u65b0\u578b\u78b1\u57fa\u7f16\u8f91\u5668ARTbase-A1\u2122\u5df2\u7ecf\u83b7\u5f97\u7f8e\u56fd\u4e13\u5229\u6388\u6743\u3002<\/p>\n

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\u5546\u52a1\u5408\u4f5c: Accuredit@accuredit.com<\/a>
\u5a92\u4f53\u8054\u7edc: tingting.zhang@accuredit.com<\/a><\/p>\n

SOURCE \u9510\u6b63\u57fa\u56e0\uff08\u82cf\u5dde\uff09\u6709\u9650\u516c\u53f8<\/p>","protected":false},"excerpt":{"rendered":"

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ASGCT\u6210\u7acb\u4e8e1996\u5e74\uff0c\u662f\u5168\u7403\u57fa\u56e0\u4e0e\u7ec6\u80de\u6cbb\u7597\u9886\u57df\u6700\u5927\u7684\u4e13\u4e1a\u6027\u975e\u8425\u5229\u533b\u5b66\u548c\u79d1\u5b66\u7ec4\u7ec7\uff0c\u5728\u5168\u7403\u62e5\u6709\u8d85\u8fc75000\u540d\u6210\u5458\u3002ASGCT\u5e74\u4f1a\u662f\u5168\u7403\u57fa\u56e0\u4e0e\u7ec6\u80de\u6cbb\u7597\u9886\u57df\u89c4\u6a21\u6700\u5927\u3001\u6700\u5177\u6743\u5a01\u6027\u7684\u5b66\u672f\u4f1a\u8bae\u3002 \u53e3\u5934\u62a5\u544a\uff1a \u6807\u9898\uff1aART001: Development and Interim Clinical Outcomes of a CRISPR-Based In Vivo Gene-Editing Therapy for Hereditary ATTR \/ ART001:\u57fa\u4e8eCRISPR\u6280\u672f\u7684\u4f53\u5185\u57fa\u56e0\u7f16\u8f91\u7597\u6cd5\u6cbb\u7597\u8f6c\u7532\u72b6\u817a\u7d20\u86cb\u767d\u6dc0\u7c89\u6837\u53d8\u6027\uff08ATTR\uff09\u7684\u6700\u65b0\u4e34\u5e8a\u8fdb\u5c55\u62a5\u544a\u65f6\u95f4\uff1a2025\u5e745\u670816\u65e5\uff08\u661f\u671f\u4e94\uff09\u4e0b\u53485:15-5:30\uff08\u7f8e\u56fd\u4e2d\u90e8\u65f6\u95f4\uff09\u5730\u70b9\uff1a393-396\u5385\u6458\u8981\u7f16\u53f7\uff1aAMA434 \u6d77\u62a5\u5c55\u793a\uff1a \u6807\u9898\uff1a Efficacy and Safety of ART002, a Single-dose Gene Editing Therapy, in Patients with Severe Heterozygous Familial Hypercholesterolemia \/ \u4f53\u5185\u57fa\u56e0\u7f16\u8f91\u7597\u6cd5ART002\u9488\u5bf9\u4e25\u91cdHeFH\u60a3\u8005\u3001\u5355\u6b21\u7ed9\u836f\u5b89\u5168\u6027\u4e0e\u6709\u6548\u6027\u7684\u4e34\u5e8a\u6570\u636e\u6d77\u62a5\u5c55\u793a\u65f6\u95f4\uff1a2025\u5e745\u670813\u65e5\uff08\u661f\u671f\u4e8c\uff09\u4e0b\u53486:00-7:30\uff08\u7f8e\u56fd\u4e2d\u90e8\u65f6\u95f4\uff09\u5730\u70b9\uff1a\u6d77\u62a5\u5c55\u793a\u5385 Hall I2\u6458\u8981\u7f16\u53f7\uff1aAMA562 \u6807\u9898\uff1aEngineering TadA-Derived Base […]<\/p>\n","protected":false},"author":0,"featured_media":10901,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[25],"tags":[],"class_list":["post-10900","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-pr-newswire"],"yoast_head":"\n\u9510\u6b63\u57fa\u56e0\u91cd\u78c5\u4ea7\u54c1\u548c\u5e73\u53f0\u4eae\u76f82025 ASGCT\u5e74\u4f1a - Money Compass CN<\/title>\n<meta name=\"robots\" content=\"index, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<link rel=\"canonical\" href=\"http:\/\/moneycompass.com.my\/cn\/\u9510\u6b63\u57fa\u56e0\u91cd\u78c5\u4ea7\u54c1\u548c\u5e73\u53f0\u4eae\u76f82025-asgct\u5e74\u4f1a\/\" \/>\n<meta property=\"og:locale\" content=\"en_US\" \/>\n<meta property=\"og:type\" content=\"article\" \/>\n<meta property=\"og:title\" content=\"\u9510\u6b63\u57fa\u56e0\u91cd\u78c5\u4ea7\u54c1\u548c\u5e73\u53f0\u4eae\u76f82025 ASGCT\u5e74\u4f1a - Money Compass CN\" \/>\n<meta property=\"og:description\" content=\"\u82cf\u5dde2025\u5e745\u670812\u65e5 \/\u7f8e\u901a\u793e\/ — 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ASGCT\u6210\u7acb\u4e8e1996\u5e74\uff0c\u662f\u5168\u7403\u57fa\u56e0\u4e0e\u7ec6\u80de\u6cbb\u7597\u9886\u57df\u6700\u5927\u7684\u4e13\u4e1a\u6027\u975e\u8425\u5229\u533b\u5b66\u548c\u79d1\u5b66\u7ec4\u7ec7\uff0c\u5728\u5168\u7403\u62e5\u6709\u8d85\u8fc75000\u540d\u6210\u5458\u3002ASGCT\u5e74\u4f1a\u662f\u5168\u7403\u57fa\u56e0\u4e0e\u7ec6\u80de\u6cbb\u7597\u9886\u57df\u89c4\u6a21\u6700\u5927\u3001\u6700\u5177\u6743\u5a01\u6027\u7684\u5b66\u672f\u4f1a\u8bae\u3002 \u53e3\u5934\u62a5\u544a\uff1a \u6807\u9898\uff1aART001: Development and Interim Clinical Outcomes of a CRISPR-Based In Vivo Gene-Editing Therapy for Hereditary ATTR \/ 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