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(RBD4059)<\/p>\n<p>Vortosiran\u662f\u745e\u535a\u751f\u7269\u57fa\u4e8eRiboGalSTAR\u2122\u809d\u9776\u5411\u6280\u672f\u5e73\u53f0\u81ea\u4e3b\u7814\u53d1\u7684\u5168\u7403\u9996\u521b\u9776\u5411FXI\u7684siRNA\u836f\u7269\uff0c\u901a\u8fc7\u7279\u5f02\u6027\u6291\u5236FXI\u57fa\u56e0\u8868\u8fbe\uff0c\u963b\u65ad\u5185\u6e90\u6027\u51dd\u8840\u9014\u5f84\u6fc0\u6d3b\uff0c\u5b9e\u73b0\u7cbe\u51c6\u7684\u6297\u51dd\u4e0e\u6297\u8840\u6813\u4f5c\u7528\u3002\u4eba\u7c7b\u9057\u4f20\u5b66\u7814\u7a76\u8868\u660e\uff0cFXI\u6c34\u5e73\u5929\u7136\u504f\u4f4e\u7684\u4eba\u7fa4\u7f79\u60a3\u8840\u6813\u6027\u75be\u75c5\u6982\u7387\u8f83\u4f4e\uff0c\u4e14\u4e0d\u4f1a\u589e\u52a0\u81ea\u53d1\u6027\u51fa\u8840\u98ce\u9669\u3002\u56e0\u6b64\uff0cFXI\u6291\u5236\u5df2\u6210\u4e3a\u5f53\u524d\u6781\u5177\u524d\u666f\u7684\u6f5c\u5728\u6cbb\u7597\u624b\u6bb5\uff0c\u65e2\u80fd\u6709\u6548\u9884\u9632\u8840\u6813\u5f62\u6210\uff0c\u540c\u65f6\u76f8\u8f83\u4e8e\u73b0\u6709\u6297\u51dd\u7597\u6cd5\u5177\u6709\u66f4\u9ad8\u7684\u5b89\u5168\u6027\u3002<\/p>\n<p>\u5173\u4e8e\u745e\u535a\u751f\u7269\u53ca\u745e\u535a\u56fd\u9645\u7814\u53d1\u4e2d\u5fc3<\/p>\n<p>\u82cf\u5dde\u745e\u535a\u751f\u7269\u6280\u672f\u80a1\u4efd\u6709\u9650\u516c\u53f8 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